3 ms·
FTA: They found cyclodextrin and initially tried using it in oral doses, which is known to be safe. However, the chemical couldn’t effectively rea
by aaronbrethorst 11y ago
FTA:
They found cyclodextrin and initially tried using it in
oral doses, which is known to be safe. However, the
chemical couldn’t effectively reach the brain that way.
The couple made headlines with their tireless efforts to
get drug companies, the FDA, and doctors to let them try
out intravenous treatments of cyclodextrin for their
twins—and they won. Regular treatments gradually
improved—although didn’t cure—the twins’ conditions.
Cyclodextrin is now in clinical trials to treat other
kids with NPC.
- dekhn 11y agoThis interesting approach just raises more questions than it answers; experiments with sample size n=1 being run by non-medically trained individuals are unorthodox and generally suspect in the modern medical climate.
- aaronbrethorst 11y agohere's another experiment for you that I've run on myself: When I consume products that contain wheat, I feel sick. When I don't, I feel fine. Sample size n=1, and I am not medically trained. What conclusions, if any, do you think I can draw from my experience?
- actaeon169 11y agoClearly, I need to stop eating wheat.
- dekhn 11y agoI don't know, did you control for placebo effects? Did you verify there isn't something else in those products that makes you feel sick? Science is hard. Control experiments are key.