It is exciting! As others in the thread are saying, the cost of individuals with severe rare diseases are also very high. Here’s a recent attempt at quantifyin

It is exciting! As others in the thread are saying, the cost of individuals with severe rare diseases are also very high. Here’s a recent attempt at quantifying the costs across all rare disease: https://chiesirarediseases.com/assets/pdf/chiesiglobalrarediseases.whitepaper-feb.-2022_production-proof.pdf https://chiesirarediseases.com/assets/pdf/chiesiglobalraredi...