3 ms·
The experiment: "The U.S. Food and Drug Administration (FDA) has given the go-ahead for the first-in-human dosing of Cure Rare Disease’s (CRD) investigational
by eternalban 4y ago
The experiment:
"The U.S. Food and Drug Administration (FDA) has given the go-ahead for the first-in-human dosing of Cure Rare Disease’s (CRD) investigational genome-editing therapeutic for Duchenne muscular dystrophy (DMD).
"Dosing of a single patient with the treatment, dubbed CRD-TMH-001, will happen soon at the University of Massachusetts Chan Medical School."
https://musculardystrophynews.com/news/crd-gene-editing-therapy-planned-dmd-patient-fda-approval/ https://musculardystrophynews.com/news/crd-gene-editing-ther...