4 ms·
Death in CRISPR gene therapy study sparks search for answers
- eternalban 4y agoThe experiment: "The U.S. Food and Drug Administration (FDA) has given the go-ahead for the first-in-human dosing of Cure Rare Disease’s (CRD) investigational genome-editing therapeutic for Duchenne muscular dystrophy (DMD). "Dosing of a single patient with the treatment, dubbed CRD-TMH-001, will happen soon at the University of Massachusetts Chan Medical School." https://musculardystrophynews.com/news/crd-gene-editing-therapy-planned-dmd-patient-fda-approval/ https://musculardystrophynews.com/news/crd-gene-editing-ther...
- yawnxyz 4y ago"At this point, it's unclear whether Horgan received the treatment and whether CRISPR, other aspects of the study or the disease itself contributed to his death" Maybe they got killed in a school shooting and it's used to cast doubt on this treatment? Absurd to write the headline and publish the article before making the connection.
- eternalban 4y agoI thought that too, but the people involved (CRD org) themselves have a page up about it, and that too is short on details. If it was definitely unrelated, they would note it. https://www.cureraredisease.org/blog-posts/to-our-community-an-update-on-our-crd-tmh-001-clinical-trial https://www.cureraredisease.org/blog-posts/to-our-community-...