4 ms·
Depending on your defect, CF can either under-produce CFTR, produce deficient CFTR, or produce no CFTR. I’d imagine each of these scenarios has different viabil
by gfodor 6y ago
Depending on your defect, CF can either under-produce CFTR, produce deficient CFTR, or produce no CFTR. I’d imagine each of these scenarios has different viability for mRNA theraputics.