3 ms·
So how do they get the crispr into the cell and into the cell nucleus? Would fixing scd be all or nothing?
by mrfusion 6y ago
So how do they get the crispr into the cell and into the cell nucleus? Would fixing scd be all or nothing?
- meepmorp 6y agoThe treatment is basically a bone marrow transplant, which would typically use donor cells from another person; CRISPR lets you use the patient's marrow instead, hopefully reducing rejection and other issues. You extract marrow and CRISPR it to get rid of the problem gene. Then you kill off all of the bone marrow in the patient, and replace it with the new stuff. That's a cure.