3 ms·

This treatment modifies the adult hemoglobin gene.

• refurb 6y ago
  That's what I get for not reading the article. But the point stands on correcting genetics for hematopoetic cells. It's possible to fix a small number of cells, then reimplant (often depleting the cells in the person first) and they will replicate. Easier than trying to fix the cells in a solid organ.