2 ms·
There are almost certainly homozygous recessive genetic diseases that can be treated if a subset of cells are able to replace the deficient enzyme. Biopsy some
by dnautics 6y ago
There are almost certainly homozygous recessive genetic diseases that can be treated if a subset of cells are able to replace the deficient enzyme.
Biopsy some cells, treat with CRISPR, return the cells.
I'm pretty on the record about CRISPR being overhyped, but to say nothing will ever be cured by CRISPR is too far.