3 ms·
The strategy they used speaks exactly to your point. The diseases were not "cured" in the sense that these people were brought back to a generic baseline. That
by dougmwne 6y ago
The strategy they used speaks exactly to your point. The diseases were not "cured" in the sense that these people were brought back to a generic baseline. That very well may have required a complex series of edits that are well beyond what is currently possible. Instead, they focused on a clever workaround that was simpler to implement, reactivating fetal hemoglobin. That's how they were able to cure two different diseases with the same gene edit.
So you have a much larger pool of genetic and non-genetic diseases that can be cured now. For example if someone had low lung function due to lung scarring, this might be an interesting treatment to look at.