3 ms·

Here’s hoping the cures come in before it kills me :-P Got high hopes for IONIS-HTTRx

• higginsc 8y ago
  Hoping for you too. It's in my mom's side of my family. I'm fortunate that my mom didn't inherit, but it's a large family so many loved ones weren't so lucky. That's why I studied biochemistry and neuroscience and got a PhD in drug discovery. Unfortunately my adolescent passion met the realities of real world of biomedical research, and now I work at FAANG. I still hold out hope that others will find a treatment someday for people like you and my family.
• modusoperandi 8y ago
  Wife has a CAG of 45. We're nearby a city center that is part of the trial and it seems like she's met all the criteria to be included so we're hopeful. Not looking forward to the monthly or bi-monthly lumbar punctures but maybe it will postpone some of her symptoms from getting worse.
  • peteretep 8y ago
    Good luck! Hopefully she’s young enough that she’ll some less invasive treatments come to market too