3 ms·
Blood disorder cured – a first for gene therapy
- po 16y agoThese stories of the work gene therapy researchers are doing remind me of trying to work on someone else's code, with no unit tests. You change one thing, which you think does what you want it to, but you don't really know. Nerve racking.
- CapitalistCartr 16y agoEspecially with people's lives at stake, a la Thalidomide.
- carbocation 16y agoI thought that Leber's congenital amaurosis was the first disorder to be cured via gene therapy.
- knowledgesale 16y ago"The first approved gene therapy case in the United States took place on September 14, 1990, at the National Institute of Health. It was performed on a four year old girl named Ashanti DeSilva. It was a treatment for a genetic defect that left her with an Immune System deficiency. The effects were only temporary, but successful (Boylan 313)." Wikipedia article on Gene therapy: http://en.wikipedia.org/wiki/Gene_therapy http://en.wikipedia.org/wiki/Gene_therapy